Sickle cell anemia, 3D illustration. Clumps of sickle cell block the blood vessel

Sickle Cell Disease Advisory Committee - Final Agenda, January 29, 2024




10:00am-10:15am: Welcome and General Introductions:

Marsha Treadwell J, PhD, University of California, San Francisco, CA, SCDAC Chair
Julie Panepinto, MD, MSPH, Director, DBDR, NHLBI, SCDAC Executive Secretary
Traci Mondoro, PhD, Chief, Translational Blood Sciences and Resource Branch, NHLBI
Juan Salomon, MS, PMP, Cure Sickle Cell Initiative Coordinator, NHLBI
Idalia Yabe, PhD, Program Officer, NHLBI

10:15am-11:15am: NHLBI SCD Program Updates

  • 10:15-10:30am NHLBI Clinical Trial mechanisms
    Speaker: Andrei Kindzelski, MD, PhD
  • 10:30-10:45am Overview of Sickle Cell Programs including Updates on the Portfolio
    Speaker: Traci Mondoro, PhD
  • 10:45-11:15am Discussion

11:15am-11:25am: Break

11:25-1:00pm: Leveraging Networks to Conduct Successful Clinical Trials in Sickle Cell Disease:

  • 11:25-11:30am: Introduction to guest speakers from networks
    Traci Mondoro, PhD
  • 11:30am-11:45pm: PECARN
    Speaker: Andrei Kindzelski, MD, PhD
  • 11:45pm-12:00pm: NICHD neonatal network
    Speaker: Nahida Chakhtoura, MD (or designee)
  • 12:00pm-12:15pm: BMT Clinical Trials Network
    Speaker: Nancy DiFronzo, PhD
  • 12:15-1:00pm: Q&A

1:00pm-1:30pm: Lunch Break

1:30pm-2:50pm: General Discussion & Committee Recommendations