Sickle Cell Disease

Prevention and treatment of complications, including pain crises and stroke; differences in how patients respond to treatment; improved stem cell transplant procedures; and new genetic therapies to treat and cure sickle cell disease.

Program Officers

Nahed El Kassar, M.D., Ph.D.
Hematologic clinical trials; Women’s health; HSCT late effects
Pankaj Qasba, Ph.D.
Hemoglobinopathies; genetic therapies; genomics; systems biology